Amy Cohen is running the New York City Marathon despite living with the painful effects of sickle cell disease.

A Phase 1b clinical trial testing pociredir in adults with sickle cell disease has completed enrollment of its high-dose ...

Seven years after the first gene-edited babies were revealed, biotech startup Manhattan Genomics is reviving the idea of ...

Manhattan Genomics is advancing next-generation medical technologies to correct harmful mutations at the embryonic stage. The company's singular mission is to prevent severe inherited conditions, such ...

SICKLE cell disease is a disease that affects people across the world. This disease affects a wide range of nations and ethnic groups. It is a genetic disorder that results from receiving the sickle ...

After four years of battling a severe blood disease, five-year-old Zion Ortiz is finally free of sickle cell anemia.

Announced encouraging results in July 2025 from the 12 mg dose cohort of the Phase 1b PIONEER trial of pociredir in sickle cell disease (SCD) ― ...

Disc Medicine is planning to launch a trial by year's end to test DISC-3405, its treatment candidate for iron overload, in ...

New research reveals how complex interactions between genetic variants can explain different outcomes in disorders like ...

Twenty-month-old Vida Rodriguez is the reason her 7-year-old sister, Alessia, is playing at home — instead of lying in a ...

Having expanded access to quantitative hemoglobin variant testing in 40 countries, Hemex is now also setting its sights on the US and Europe.

One of the most revolutionary tools in cutting-edge medicine is a molecular scalpel so precise that it can modify defective DNA and fix genetic diseases like sickle cell anemia, and chronic disorders ...