Limited treatment options and access to care often challenge patients with Friedreich’s ataxia. So, on Sept. 17, the ...

The FDA’s mid-November decision on Biohaven’s spinocerebellar ataxia treatment could redefine rare disease approvals and ...

Design Therapeutics, Inc. (($DSGN)) announced an update on their ongoing clinical study. Study Overview: Design Therapeutics, Inc. is conducting a ...

As momentum for Biogen’s newer drugs for neurological disorders builds at a slow and steady pace, it appears that the company ...

Larimar Therapeutics, Inc. (($LRMR)) announced an update on their ongoing clinical study. Larimar Therapeutics, Inc. is conducting a Phase 1 ...

In a small study, 80% of testicular cancer patients developed paraneoplastic neurologic syndromes before their cancer diagnosis — highlighting a need for early detection.

(Nasdaq: QNCX), a late-stage biotechnology company dedicated to unlocking the power of a patient’s own biology for the treatment of rare diseases, today announced the poster presentation of ...

The FDA has issued an Emergency Use Authorization (EUA) for an animal drug to treat dogs and puppies infected with the ...

Through its collaboration with Variational AI, Rakovina Therapeutics utilized the Enki™ generative AI platform to identify novel small-molecule candidates predicted to meet a defined target product ...

Biogen Inc. ( BIIB) Q3 2025 Earnings Call October 30, 2025 8:30 AM EDT Good morning. My name is Cynthia, and I will be your conference operator today. At this time, I would like to welcome everyone to ...

Protests were expected to run throughout the day Oct. 18 in Michigan in places as far as the Upper Peninsula as well as in ...