A one-time gene-editing therapy, exagamglogene autotemcel (exa-cel), has demonstrated sustained and clinically meaningful ...
People are often encouraged to “know their status,” however this healthy habit can be applied to more than just safe-sex practices. Although they are not the only community who suffers with sickle ...
Amy Cohen is running the New York City Marathon despite living with the painful effects of sickle cell disease.
Sickle cell disease refers to a group of genetic diseases that impact a protein that ferries oxygen through the blood. That protein is called hemoglobin, and in sickle cell disease, aberrant ...
Vertex Pharmaceuticals Inc. (($VRTX)) announced an update on their ongoing clinical study. Vertex Pharmaceuticals Inc. is conducting a Phase 3 ...
Gene therapy has the potential to dramatically benefit patients with genetic blood disorders, but a small study on participants in a clinical trial for sickle cell disease suggests that a key process ...
Azim, MD, MS, Division Chief Transplant and Cell Therapy/Hematological malignancies at Loma Linda University (LLU) Cancer ...
Sickle cell disease (SCD) is an inherited disorder that affects over 100,000 people in the United States, according to the Sickle Cell Disease Association of America, of that number, the Centers for ...
Detroit — Pain is familiar and far from predictable for people such as Medjie Pascal-Harris, a Detroiter who lives with sickle cell disease, an inherited blood disorder that cuts 20-30 years off the ...
At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...
Life expectancy has soared and interest in the disease is growing, but breakthrough gene therapies are extraordinarily ...
The federal approval of two new gene therapy treatments for sickle cell disease has created a groundbreaking option for patients. Across the nation, it is unknown how many suffer from the disease, but ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback